Kate Williams

Associate Professor in Translational Medicine

• Research
• Impact, Enterprise and Outreach
• Esteem Factors
• International Collaborators
• National Collaborators
• Publications

• Funding from medical charities for muscular dystrophy and diabetes research
• Engineering viruses to deliver large transgenes to augment muscle mass and function
• Developing antisense exon skipping technologies to augment muscle mass and function
• Developing peptide conjugates to increase gene medicine delivery or tissue tropism
• Assessing impact of muscle loss associated with metabolic diseases
• Developing gene medicines for metabolic diseases

Member of the

Impact, Enterprise and Outreach

• Scottish parliamentary debate
• UK parliamentary task force member for fast tracking gene medicines for rare diseases
• European Medicine Agency 'clinical endpoints of trials' framework document
• Interviews with BBC Radio 5 Live and the Naked scientist

Esteem Factors

• Scientific editorial board for the journal 'Human Gene Therapy Methods'.
• Expert grant reviewer for 'Health Research Board, Ireland', 'Exerc-IND 2012', 'Association Française contre les Myopathies', 'Telethon of Italy', 'Myotubular Trust' and ad-hoc exert grant reviewer for other national and international funding agencies.
• Chair of Scientific Advisory Board for medical charity 'Joining Jack'
• Local organiser of the 2013 British Society of Gene Therapy meeting
• International Duchenne Exon Skipping Consortium Member

International Collaborators

• Prof. Greg Verdine, Harvard, US
• Dr. Rob Kotin, NIH Bethesda, US
• Dr. Luis Garcia, Université de Versailles Saint Quentin en Yvelines, France

National Collaborators

• Dr. Mark Cleasby, Royal Veterinary School, London
• Prof. Raj Mookerjee, University College, London
• Dr. Gautum Mehta, University College, London
• Prof. Dominic Wells, Royal Veterinary School, London